Molecular Therapy

Title Publication Date Language Citations
Learning to lock down genetic diseases without throwing away the key2023/07/01English
Adverse event reporting to US Food and Drug Administration and risk evaluation and mitigation strategies2023/04/01English
Preclinical evaluation of ADVM-062, a novel intravitreal gene therapy vector for the treatment of blue cone monochromacy2023/07/01English
Tailoring CAR T cell technology for T cell leukemia2023/03/01English
Advanced gene-editing strategy for epidermolysis bullosa simplex2024/02/01English
Current RNA strategies in treating cardiovascular diseases2024/03/01English
Knockdown of calpain1 in lumbar motoneurons reduces spasticity after spinal cord injury in adult rats2024/04/01English
Innovative stem cell-based strategies for corneal wound healing: A step forward2023/08/01English
In this issue2023/08/01English
Efficient T cell adoptive transfer in lymphoreplete hosts mediated by transient activation of Stat5 signaling2023/09/01English
Bypassing the cytokine sink: IL-2-independent IL-2 receptor signaling2023/08/01English
A fond farewell2023/02/01English
Of LAMA3 and LAMB3: A novel gene therapy for epidermolysis bullosa2024/04/01English
Expanding strategies to resolve psoriasis-like inflammation: Non-canonical NF-κB signaling controls IL-23 production in dendritic cells2024/04/01English
In this issue2024/04/01English
Three recent breakthroughs in CAR T cells for the treatment of glioblastoma: Is it the light at the end of the tunnel?2024/04/01English
Bis-2′-F-cGSASMP Isomers Encapsulated in Cytidinyl/Cationic Lipids Act as Potent in situ Autologous Tumor Vaccines2024/04/01English
Oral Abstracts2024/04/01English
VCAM-targeting lipid platform brings new hope to the treatment of ischemic stroke2024/04/01English
Defining mesenchymal stem/stromal cell-induced myeloid-derived suppressor cells using single-cell transcriptomics2024/04/01English
Switch of ELF3 and ATF4 transcriptional axis programs the amino acid insufficiency-linked epithelial-to-mesenchymal transition2024/04/01English
DRP1 bridges complement component C5a and podocyte injury in lupus nephritis2024/04/01English
Metachromatic leukodystrophy: A story of hope woven from sorrow2024/04/01English
Evolution of the clinical-stage hyperactive TcBuster transposase as a platform for robust non-viral production of adoptive cellular therapies2024/04/01English
Preclinical evaluation of KH631, a novel rAAV8 gene therapy product for neovascular age-related macular degeneration2023/11/01English
Response to: DNA transposon mechanisms and pathways of genotoxicity2023/10/01English
Engineered arylsulfatase A with increased activity, stability and brain delivery for therapy of metachromatic leukodystrophy2023/10/01English
Chemerin triggers migration of a CD8 T cell subset with natural killer cell functions2023/10/01English
Atractylodinol prevents pulmonary fibrosis through inhibiting TGF-β receptor 1 recycling by stabilizing vimentin2023/10/01English
AAV9-mediated SH3TC2 gene replacement therapy targeted to Schwann cells for the treatment of CMT4C2023/11/01English