Title	Publication Date	Language	Citations
Rapid and highly efficient transduction by double-stranded adeno-associated virus vectors in vitro and in vivo	2003/11/17	English	307
Development of a novel systemic gene delivery system for cancer therapy with a tumor-specific cleavable PEG-lipid	2006/08/17	English	299
Chemical modification and design of anti-miRNA oligonucleotides	2011/07/14	English	296
Factors affecting blood clearance and in vivo distribution of polyelectrolyte complexes for gene delivery	1999/04/01	English	289
Development of safe and efficient novel nonviral gene transfer using ultrasound: enhancement of transfection efficiency of naked plasmid DNA in skeletal muscle	2002/03/01	English	286
MicroRNA therapeutics	2011/04/28	English	282
Gene therapy progress and prospects: non-viral gene therapy by systemic delivery	2006/09/01	English	279
Efficacy and long-term safety of alipogene tiparvovec (AAV1-LPLS447X) gene therapy for lipoprotein lipase deficiency: an open-label trial	2012/06/21	English	273
Improved chitosan-mediated gene delivery based on easily dissociated chitosan polyplexes of highly defined chitosan oligomers	2004/07/22	English	269
Human mesenchymal stem cells: from basic biology to clinical applications	2007/11/08	English	267
Progress and prospects: naked DNA gene transfer and therapy	2003/03/01	English	264
Polyethylenimine-based intravenous delivery of transgenes to mouse lung	1998/09/01	English	262
Electropermeabilization of skeletal muscle enhances gene transfer in vivo	1999/04/01	English	261
A novel siRNA-lipoplex technology for RNA interference in the mouse vascular endothelium	2006/04/20	English	259
Immune response to green fluorescent protein: implications for gene therapy	1999/07/01	English	258
Global CNS gene delivery and evasion of anti-AAV-neutralizing antibodies by intrathecal AAV administration in non-human primates	2013/01/10	English	251
Gene therapy progress and prospects: Ultrasound for gene transfer	2007/03/01	English	250
Dynamic changes in the characteristics of cationic lipidic vectors after exposure to mouse serum: implications for intravenous lipofection	1999/04/01	English	247
Evaluation of polyether-polyethyleneimine graft copolymers as gene transfer agents	2000/01/01	English	246
Intracellular trafficking of nonviral vectors	2005/08/04	English	244
Treatment of experimental equine osteoarthritis by in vivo delivery of the equine interleukin-1 receptor antagonist gene	2002/01/01	English	243
Anti-miRNA oligonucleotides (AMOs): ammunition to target miRNAs implicated in human disease?	2005/09/29	English	243
Characterization of cationic lipid-protamine–DNA (LPD) complexes for intravenous gene delivery	1998/07/01	English	242
Polyethylenimine/DNA complexes shielded by transferrin target gene expression to tumors after systemic application	2001/01/01	English	242
Coupling of cell-binding ligands to polyethylenimine for targeted gene delivery	1997/05/01	English	241
Human synapsin 1 gene promoter confers highly neuron-specific long-term transgene expression from an adenoviral vector in the adult rat brain depending on the transduced area	2003/02/01	English	240
Nanotechnologies in delivery of mRNA therapeutics using nonviral vector-based delivery systems	2017/01/17	English	239
The silent treatment: siRNAs as small molecule drugs	2006/01/05	English	238
Clinical research results with dl1520 (Onyx-015), a replication-selective adenovirus for the treatment of cancer: what have we learned?	2001/01/01	English	237
Microbubble-enhanced ultrasound for vascular gene delivery	2000/12/01	English	231