Titel	Veröffentlichungsdatum	Sprache	Zitate
Design, construction and in vivo functional assessment of a hinge truncated sFLT01	2022/09/16	English
Author Index	2001/10/01	English
Non-coding RNAs and the advent of new directions in therapeutics	2011/12/01	English
A vaccine that delivers rather than induces antibodies	2009/09/17	English
Commenting on communicator RNA	2011/08/18	English
Precision-guided genetic ordnance: new developments in receptor targeting of recombinant AAV	2003/11/03	English
Clinical trials: The sensitizing side of Onyx-015	2005/01/13	English
Targeting ‘horror autotoxicus’ by gene therapy: results, challenges and the future	2003/05/01	English
Fabry Disease: Vector Divergence to Convergence?	2003/08/01	English
In vivo splenic CD11c cells downregulate CD4 T-cell response thereby decreasing systemic immunity to gene-modified tumour cell vaccine	2007/08/16	English
Cardiac gene therapy: Kick-starting calcium cycling in rats	2005/02/24	English
AAV9-mediated engineering of autotransplanted kidney of non-human primates	2017/03/27	English
Are genetically modified protozoa eligible for ATMP status? Concerning the legal categorization of an oncolytic protozoan drug candidate	2024/03/01	English
A multinational survey of potential participant perspectives on ocular gene therapy	2024/04/02	English
Distributional comparison of different AAV vectors after unilateral cochlear administration	2023/12/14	English
Prednisolone and rapamycin reduce the plasma cell gene signature and may improve AAV gene therapy in cynomolgus macaques	2023/10/13	English
Modeling Glutaric Aciduria Type I in human neuroblastoma cells recapitulates neuronal damage that can be rescued by gene replacement	2023/11/20	English
A shedding analysis after AAV8 CNS injection revealed fragmented viral DNA without evidence of functional AAV particles in mice	2024/03/12	English
Precision ophthalmology: a call for Africa not to be left in the dark	2024/03/22	English
Advancing rare disease treatment: EMA’s decade-long insights into engineered adoptive cell therapy for rare cancers and orphan designation	2024/03/14	English
Adeno-associated virus genome quantification with amplification-free CRISPR-Cas12a	2024/03/25	English
Development of a stable Sf9 insect cell line to produce VSV-G pseudotyped baculoviruses	2024/01/26	English
Preclinical dose response study shows NR2E3 can attenuate retinal degeneration in the retinitis pigmentosa mouse model RhoP23H+/−	2024/01/26	English
Sildenafil increases AAV9 transduction after a systemic administration and enhances AAV9-dystrophin therapeutic effect in mdx mice	2023/07/27	English
Immunobiology of a rationally-designed AAV2 capsid following intravitreal delivery in mice	2023/06/29	English
Long-term benefits of hematopoietic stem cell-based macrophage/microglia delivery of GDNF to the CNS in a mouse model of Parkinson’s disease	2024/04/16	English
Analytical characterization of full, intermediate, and empty AAV capsids	2024/02/19	English
Artificial microRNA suppresses C9ORF72 variants and decreases toxic dipeptide repeat proteins in vivo	2023/09/26	English
Biodistribution of lentiviral transduced adipose-derived stem cells for “ex-vivo” regional gene therapy for bone repair	2023/08/11	English
Long-term effects of a fat-directed FGF21 gene therapy in aged female mice	2023/09/12	English