Title	Publication Date	Language	Citations
Adenoviral Vector-Delivered Pigment Epithelium-Derived Factor for Neovascular Age-Related Macular Degeneration: Results of a Phase I Clinical Trial	2006/02/01	English	204
Adeno-Associated Virus (AAV) Serotype 9 Provides Global Cardiac Gene Transfer Superior to AAV1, AAV6, AAV7, and AAV8 in the Mouse and Rat	2008/12/01	English	203
Self-Inactivating Lentiviral Vectors with Enhanced Transgene Expression as Potential Gene Transfer System in Parkinson's Disease	2000/01/01	English	203
Immunological Aspects of Allogeneic Mesenchymal Stem Cell Therapies	2010/12/01	English	203
HumanRPE65Gene Therapy for Leber Congenital Amaurosis: Persistence of Early Visual Improvements and Safety at 1 Year	2009/09/01	English	200
Lentiviral-Mediated RNA Interference	2002/12/10	English	197
Redirecting Migration of T Cells to Chemokine Secreted from Tumors by Genetic Modification with CXCR2	2002/11/01	English	197
Overcoming the Innate Immune Response to Small Interfering RNA	2008/02/01	English	197
Characterization of Cationic Liposome-Mediated Gene TransferIn Vivoby Intravenous Administration	1997/09/01	English	195
In Situ Gene Therapy for Adenocarcinoma of the Prostate: A Phase I Clinical Trial	1999/05/01	English	193
Herpes Simplex Virus as an in Situ Cancer Vaccine for the Induction of Specific Anti-Tumor Immunity	1999/02/10	English	192
Enhanced Expression of Transgenes from Adeno-Associated Virus Vectors with the Woodchuck Hepatitis Virus Posttranscriptional Regulatory Element: Implications for Gene Therapy	1999/09/20	English	191
Compacted DNA Nanoparticles Administered to the Nasal Mucosa of Cystic Fibrosis Subjects Are Safe and Demonstrate Partial to Complete Cystic Fibrosis Transmembrane Regulator Reconstitution	2004/12/01	English	190
Oligonucleotide Therapies: The Past and the Present	2015/08/01	English	190
Factors Influencing Recombinant Adeno-Associated Virus Production	1998/03/20	English	190
Adeno-Associated Virus-Based Gene Therapy for CNS Diseases	2016/07/01	English	189
Direct Gene Transfer into Nonhuman Primate Myofibers In Vivo	1992/02/01	English	187
The First Approved Gene Therapy Product for Cancer Ad-p53(Gendicine): 12 Years in the Clinic	2018/02/01	English	186
Intracerebral Administration of Adeno-Associated Viral Vector Serotype rh.10 Carrying Human SGSH and SUMF1 cDNAs in Children with Mucopolysaccharidosis Type IIIA Disease: Results of a Phase I/II Trial	2014/06/01	English	185
Long-Term Evaluation of a Phase 1 Study of AADC Gene Therapy for Parkinson's Disease	2012/04/01	English	184
Evaluation of the Transfer and Expression in Mice of an Enzyme-Encoding Gene Using a Human Adenovirus Vector	1990/10/01	English	184
Fluorescent Virions: Dynamic Tracking of the Pathway of Adenoviral Gene Transfer Vectors in Living Cells	1998/02/10	English	183
Efficient Gene Delivery and Targeted Expression to HepatocytesIn Vivoby Improved Lentiviral Vectors	2002/01/20	English	183
A Novel Tumor-Specific Replication-Restricted Adenoviral Vector for Gene Therapy of Hepatocellular Carcinoma	1999/07/01	English	183
Gene Transfer In Vivo with DNA–Liposome Complexes: Safety and Acute Toxicity in Mice	1992/06/01	English	181
Acute Toxicity After High-Dose Systemic Injection of Helper-Dependent Adenoviral Vectors into Nonhuman Primates	2004/01/01	English	181
High Doses of a Helper-Dependent Adenoviral Vector Yield Supraphysiological Levels ofα1-Antitrypsin with Negligible Toxicity	1998/12/10	English	181
Gene Therapy-Directed Osteogenesis: BMP-7-Transduced Human Fibroblasts Form Bonein Vivo	2000/05/20	English	180
Adeno-Associated Virus at 50: A Golden Anniversary of Discovery, Research, and Gene Therapy Success—A Personal Perspective	2015/05/01	English	177
Repeated Aerosolized AAV-CFTR for Treatment of Cystic Fibrosis: A Randomized Placebo-Controlled Phase 2B Trial	2007/08/01	English	176