Human Gene Therapy

Title Publication Date Language Citations
The Target's the Thing2016/07/01English
Correction to: Hum Gene Ther 2016;27(6):417–4182016/07/01English
Twelfth Annual Meeting of the French Society of Cell and Gene Therapy2016/07/01English
Correction to: Hum Gene Ther 2016;27(6):436–4502016/07/01English
The Renaissance of Gene and Cell Therapy: Florence 20162016/10/01English
CRISPR-Mediated Base Editing: Promises and Challenges for a Viable Oncotherapy Strategy2023/08/01English
Assessment of Residual Full-Length SV40 Large T Antigen in Clinical-Grade Adeno-Associated Virus Vectors Produced in 293T Cells2023/08/01English
Characteristics, Recombination Methods, and Applications Progresses of Split-Cas9 System2023/07/01English
Recombinant DNA Advisory Committee Meeting March 7, 20022002/05/20English
Future Meetings of the NIH Recombinant DNA Advisory Committee (RAC) and Gene Therapy Policy Conferences (GTPC)1999/03/20English
Future Meetings of the NIH Recombinant DNA Advisory Commitee (RAC) and Gene Therapy Policy Conferences (GTPC)1999/01/01English
Future Meeting Dates and Protocol Submission Deadlines for Public Recombinant DNA Advisory Committee (RAC) Review2001/03/01English
Engineering Cells for Glucose-Sensitive Production of Insulin: Toward Genetic Reconstruction2000/02/10English
Future Meetings of the NIH Recombinant DNA Advisory Committee (RAC) and Gene Therapy Policy Conferences (GTPC)1999/09/20English
Regulatory Issues Future Meetings of the NIH Recombinant DNA Advisory Committee (RAC) and Gene Therapy Policy Conferences (GTPC)1999/03/01English
Future Meeting Dates and Protocol Submission Deadlines for Public Recombinant DNA Advisory Committee (RAC) Review2001/10/10English
Danaher Partners with Innovative Genomics Institute, Doudna, and Urnov on Beacon for CRISPR Cures2024/02/01English
A Paradox of the Field's Own Success: Unintended Challenges in Bringing Cutting-Edge Science from the Bench to the Market2024/02/01English
Pre-Existing Immunity to a Nucleic Acid Contaminant-Derived Antigen Mediates Transaminitis and Resultant Diminished Transgene Expression in a Mouse Model of Hepatic Recombinant Adeno-Associated Virus-Mediated Gene Transfer2024/03/28English
Current Status and Prospects of Viral Vector-Based Gene Therapy to Treat Kidney Diseases2024/03/01English
Combination Immunotherapy of Oncolytic Flu-Vectored Virus and Programmed Cell Death 1 Blockade Enhances Antitumor Activity in Hepatocellular Carcinoma2024/03/01English
Gutless Helper-Dependent and First-Generation HAdV5 Vectors Have Similar Mechanical Properties and Common Transduction Mechanisms2024/03/01English
Therapeutic Strategy for Fabry Disease by Intravenous Administration of Adeno-Associated Virus 9 in a Symptomatic Mouse Model2024/03/01English
Prevalence Study of Cellular Capsid-Specific Immune Responses to AAV2, 4, 5, 8, 9, and rh10 in Healthy Donors2024/04/19English
Concise Analysis of Single-Stranded DNA of Recombinant Adeno-Associated Virus By Automated Electrophoresis System2024/02/01English
Leveraging CRISPR-Cas9 for Accurate Detection of AAV-Neutralizing Antibodies: The AAV-HDR Method2024/01/19English
Activist Investor Reported to Take $1 Billion Stake in BioMarin2023/12/01English
The British Society for Gene and Cell Therapy at 20 (2003–2023)2024/01/01English
A Novel Role for the Adenovirus L4 Region 22K and 33K Proteins in Adeno-Associated Virus Production2024/01/01English
Lentiviral Gene Therapy for Mucopolysaccharidosis II with Tagged Iduronate 2-Sulfatase Prevents Life-Threatening Pathology in Peripheral Tissues But Fails to Correct Cartilage2024/04/01English